Brazilian consensus on Duchenne muscular dystrophy. Part 1: diagnosis, steroid therapy and perspectives
Arq. neuropsiquiatr; 75 (8), 2017
ABSTRACT Significant advances in the understanding and management of Duchenne muscular dystrophy (DMD) took place since international guidelines were published in 2010. Our objective was to provide an evidence-based national consensus statement for multidisciplinary care of DMD in Brazil. A combination o...
Brasil, Ensayos Clínicos como Asunto, Técnica Delphi, Medicina Basada en la Evidencia, Estudios de Seguimiento, Pruebas Genéticas, Glucocorticoides/uso terapéutico, Distrofia Muscular de Duchenne/diagnóstico, Distrofia Muscular de Duchenne/tratamiento farmacológico, Distrofia Muscular de Duchenne/genética, Grupo de Atención al Paciente, Literatura de Revisión como Asunto, Resultado del Tratamiento